| Gene symbol | LDLR | Synonyms | FH, FHC, FHCL1, LDLCQ2 | Type of gene | protein-coding |
| Chromosome | 19 | Map location | 19p13.2 | dbXrefs | |
| Gene perturbation-related omics dataset | PerturbAtlas | PertOrg | ||||
| Description | low density lipoprotein receptor | ||||
| GTO ID | GTC3786 |
| Trial ID | NCT06293729 |
| Disease | Familial Hypercholesterolemia |
| Altered gene | LDLR |
| Therapeutic/Target gene | Therapeutic gene |
| Therapy | Gene transfer |
| Treatment | NGGT006 |
| Phase | Early_Phase1 |
| Recruitment status | Not Recruiting |
| Title | A Clinical Study for the Safety and Efficacy of Intravenous Infusion of NGGT006 in Treatment of Refractory Hypercholesterolemia |
| Year | 2024 |
| Country | China |
| Company sponsor | Suzhou Municipal Hospital |
| Other ID(s) | NGGT006-P-2302 |
| Vector information | |||||||||||
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| Cohort 1 | |||||||||
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