Basic Information


GTO ID GTC3746
Trial ID NCT06243770
Disease Heart Failure
Altered gene RLN
Therapeutic/Target gene Therapeutic gene
TherapymRNA
Treatment mRNA-0184
PhasePhase1
Recruitment statusRecruiting
TitleA Phase 1, Randomized, Open-label, Multiple Ascending Dose Study to Investigate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of mRNA-0184 Administered at 2 Different Infusion Durations in Healthy Participants
Year2024
CountryAustralia
Company sponsorModernaTX, Inc.
Other ID(s)mRNA-CRTX-001
Vector information
Vectorlipid nanoparticle

Clinical Result

Cohort1: duration 1 on Day 1
Administration route intravenous infusion
Dosage mRNA-0184, duration 1 on Day 1, duration 2 on Day 22
Age Adult
Cohort2: duration 2 on Day 1
Administration route intravenous infusion
Dosage mRNA-0184, duration 2 on Day 1, duration 1 on Day 22
Age Adult

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