Basic Information


GTO ID GTC3540
Trial ID NCT05984927
Disease Age-Related Macular Degeneration
TherapyGene transfer
Treatment NG101
PhasePhase1|Phase2
Recruitment statusRecruiting
TitleA Phase 1/2a Open-label Study to Evaluate Safety, Tolerability and Preliminary Efficacy of NG101 AAV Gene Therapy in Subjects With Wet Age-Related Macular Degeneration
Year2023
CountryCanada
Company sponsorNeuracle Genetics, Inc
Other ID(s)NG101WA-01
Vector information
Vectoradeno-associated virus
Vector typenon-replicating adeno-associated virus serotype 8 (AAV8) vector

Clinical Result

Cohort1: dose level 1
Administration route subretinal injection
Dosage 1E9 vg
Age Adult, Older_Adult
Cohort2: dose level 2
Administration route subretinal injection
Dosage 3E9 vg
Age Adult, Older_Adult
Cohort3: dose level 3
Administration route subretinal injection
Dosage 8E9 vg
Age Adult, Older_Adult

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