Basic Information


GTO ID GTC3282
Trial ID NCT05659264
Disease Heart Failure
Altered gene RLN
Therapeutic/Target gene Therapeutic gene
TherapymRNA
Treatment mRNA-0184
PhasePhase1
Recruitment statusRecruiting
TitleA Phase 1, Adaptive, Open-Label, Single Ascending Dose to Single-Blind, Placebo-Controlled, Multiple Ascending Dose Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of mRNA-0184 in Participants With Chronic Heart Failure
Year2022
CountryPoland|United Kingdom|United States
Company sponsorModernaTX, Inc.
Other ID(s)mRNA-0184-P101|2022-000784-46
Vector information
Vectorlipid nanoparticle

Clinical Result

Cohort1: mRNA-0184_single dose
Administration route intravenous infusion
Dosage mRNA-0184, single dose
Age Adult, Older_Adult
Cohort2: mRNA-0184_up to 4 doses
Administration route intravenous infusion
Dosage mRNA-0184, up to 4 doses, over a treatment period of up to 16 weeks
Age Adult, Older_Adult
Cohort3: Placebo
Administration route intravenous infusion
Age Adult, Older_Adult

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