Basic Information

Gene symbol TTR Synonyms ATTR, CTS, CTS1, HEL111, HsT2651, PALB, TBPA, TTN Type of gene protein-coding
Gene perturbation-related omics dataset PerturbAtlas
Description transthyretin

GTO ID GTC2789
Trial ID NCT05040373
Disease Polyneuropathy | Transthyretin Amyloidosis
Altered gene TTR
Therapeutic/Target gene Target gene
TherapysiRNA
Treatment ALN-TTR02|ONPATTRO|patisiran
Location approved US, EU, UK, Japan, Canada, Switzerland, Brazil, China, Israel, Turkey, Australia
Recruitment statusRecruiting
TitlePatisiran-LNP Pregnancy Surveillance Program
Year2020
CountryFrance|Germany|Italy|Netherlands|Portugal|Spain|United States
Company sponsorAlnylam Pharmaceuticals
Other ID(s)ALN-TTR02-010
Vector information
Vectorlipid nanoparticle

Clinical Result

Cohort 1
Administration route None
Pts 10
Age Child, Adult, Older_Adult

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