GTO ID | GTC2710 |
Trial ID | NCT04919473 |
Disease | Retinitis Pigmentosa | Retinal Disease | Retinal Degeneration |
Altered gene | MCO |
Therapeutic/Target gene | Therapeutic gene |
Therapy | Gene transfer |
Treatment | vMCO-I|AAV2-MCO |
Phase | Phase1|Phase2 |
Recruitment status | Completed |
Title | A Phase I/IIa Open Label, Dose-Escalation Study to Evaluate the Safety and Tolerability of Intravitreal vMCO-I in Patients With Advanced Retinitis Pigmentosa |
Year | 2021 |
Country | Italy |
Company sponsor | Nanoscope Therapeutics Inc. |
Other ID(s) | NSCT/CT/18/01 |
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Cohort1: dose level 1 | |||||||||
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Cohort2: dose level 2 | |||||||||
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