Basic Information

Gene symbol NRARP Synonyms None Type of gene protein-coding
Description NOTCH regulated ankyrin repeat protein

GTO ID GTC2610
Trial ID NCT04782271
Disease Choroidal Neovascularization
Altered gene NRARP
Therapeutic/Target gene Target gene
TherapysiRNA
Treatment SYL1801
PhasePhase1
Recruitment statusCompleted
TitleSafety, Tolerability and Pharmacokinetic Profile of Different Doses of SYL1801 Ophthalmic Solution in Healthy Volunteers
Year2021
CountrySpain
Company sponsorSylentis, S.A.
Other ID(s)SYL1801_I

Clinical Result

Cohort1: dose level 1_Single dose_once daily
Administration route ophthalmic administration
Dosage SYL18001 sodium, Low dose, once daily, Single dose
Age Adult
Cohort2: dose level 2_Single dose_once daily
Administration route ophthalmic administration
Dosage SYL18001 sodium, Middle dose, once daily, Single dose
Age Adult
Cohort3: dose level 3_Single dose_once daily
Administration route ophthalmic administration
Dosage SYL18001 sodium, High dose, once daily, Single dose
Age Adult
Cohort4: dose level 3_Single dose_twice daily
Administration route ophthalmic administration
Dosage SYL18001 sodium, High dose, twice daily, Single dose
Age Adult
Cohort5: dose level 1_Multiple dose_once daily
Administration route ophthalmic administration
Dosage SYL18001 sodium, Low dose, once daily, Multiple dose
Age Adult
Cohort6: dose level 2_Multiple dose_once daily
Administration route ophthalmic administration
Dosage SYL18001 sodium, Middle dose, once daily, Multiple dose
Age Adult
Cohort7: dose level 3_Multiple dose_once daily
Administration route ophthalmic administration
Dosage SYL18001 sodium, High dose, once daily, Multiple dose
Age Adult
Cohort8: dose level 3_Multiple dose_twice daily
Administration route ophthalmic administration
Dosage SYL18001 sodium, High dose, twice daily, Multiple dose
Age Adult

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