| Gene symbol | RPGR | Synonyms | COD1, CORDX1, CRD, PCDX, RP15, RP3, XLRP3, orf15 | Type of gene | protein-coding |
| Chromosome | X | Map location | Xp11.4 | dbXrefs | |
| Description | retinitis pigmentosa GTPase regulator | ||||
| GTO ID | GTC2540 |
| Trial ID | NCT04671433 |
| Disease | Retinitis Pigmentosa |
| Altered gene | RPGR |
| Therapeutic/Target gene | Therapeutic gene |
| Therapy | Gene transfer |
| Treatment | botaretigene sparoparvovec |
| Phase | Phase3 |
| Recruitment status | Active, Not Recruiting |
| Title | Phase 3 Randomized, Controlled Study of AAV5-RPGR for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene |
| Year | 2020 |
| Country | Belgium|Canada|Denmark|France|Israel|Italy|Netherlands|Spain|Switzerland|United Kingdom|United States |
| Company sponsor | MeiraGTx UK II Ltd |
| Other ID(s) | MGT-RPGR-021|2020-002873-88 |
| Vector information | |||||||||||
|
|||||||||||
| Cohort 1 | |||||||
|
|||||||