| Gene symbol | RPGR | Synonyms | COD1, CORDX1, CRD, PCDX, RP15, RP3, XLRP3, orf15 | Type of gene | protein-coding |
| Chromosome | X | Map location | Xp11.4 | dbXrefs | |
| Description | retinitis pigmentosa GTPase regulator | ||||
| GTO ID | GTC2431 |
| Trial ID | NCT04517149 |
| Disease | Retinitis Pigmentosa |
| Altered gene | RPGR |
| Therapeutic/Target gene | Therapeutic gene |
| Therapy | Gene transfer |
| Treatment | 4D-125 |
| Phase | Phase1|Phase2 |
| Recruitment status | Active, Not Recruiting |
| Title | An Open-label, Phase 1/2 Trial of Gene Therapy 4D-125 in Males With X-linked Retinitis Pigmentosa (XLRP) Caused by Mutations in the RPGR Gene |
| Year | 2020 |
| Country | United States |
| Company sponsor | 4D Molecular Therapeutics |
| Other ID(s) | 4D-125-C001 |
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