| Gene symbol | RPGR | Synonyms | COD1, CORDX1, CRD, PCDX, RP15, RP3, XLRP3, orf15 | Type of gene | protein-coding |
| Chromosome | X | Map location | Xp11.4 | dbXrefs | |
| Description | retinitis pigmentosa GTPase regulator | ||||
| GTO ID | GTC2333 |
| Trial ID | NCT04312672 |
| Disease | Retinitis Pigmentosa |
| Altered gene | RPGR |
| Therapeutic/Target gene | Therapeutic gene |
| Therapy | Gene transfer |
| Treatment | botaretigene sparoparvovec |
| Recruitment status | Active, Not Recruiting |
| Title | Long Term Follow-Up Study of Participants Following an Open Label, Multi-Centre, Phase I/II Dose Escalation Trial of a Recombinant Adeno-Associated Virus Vector (AAV2-RPGR) for Gene Therapy of Adults and Children With X-Linked Retinitis Pigmentosa Owing to Defects in Retinitis Pigmentosa GTPase Regulator (RPGR) |
| Year | 2019 |
| Country | United Kingdom|United States |
| Company sponsor | MeiraGTx UK II Ltd |
| Other ID(s) | MGT010 |
| Vector information | |||||||||||
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| Cohort 1 | |||||||
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