Basic Information

Gene symbol TTR Synonyms ATTR, CTS, CTS1, HEL111, HsT2651, PALB, TBPA, TTN Type of gene protein-coding
Gene perturbation-related omics dataset PerturbAtlas
Description transthyretin

GTO ID GTC2306
Trial ID NCT04270058
Disease Transthyretin Amyloid Cardiomyopathy
Altered gene TTR
Therapeutic/Target gene Target gene
TherapyASO
Treatment ISIS 416858|IONIS-FXIRX|FXI-ASO|ISIS-FXI Rx|BAY2306001||BAY2306001|Fesomersen
Recruitment statusRecruiting
TitlePregnancy Surveillance Program of Women and Infants Exposed to TEGSEDI During Pregnancy
Year2020
CountryUnited States
Company sponsorAkcea Therapeutics
Other ID(s)TEG4005
Vector information
VectorNo vector was used

Clinical Result

Cohort1: inotersen
Administration route subcutaneous injection
Age Child, Adult, Older_Adult
Cohort2: No Intervention
Administration route None
Age Child, Adult, Older_Adult

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