Gene symbol | RHO | Synonyms | CSNBAD1, OPN2, RP4 | Type of gene | protein-coding |
Chromosome | 3 | Map location | 3q22.1 | dbXrefs | |
Gene perturbation-related omics dataset | PerturbAtlas | PertOrg | ||||
Description | rhodopsin |
GTO ID | GTC2206 |
Trial ID | NCT04123626 |
Disease | Retinitis Pigmentosa |
Altered gene | RHO |
Therapeutic/Target gene | Target gene |
Therapy | ASO |
Treatment | QR-1123 |
Phase | Phase1|Phase2 |
Recruitment status | Active, Not Recruiting |
Title | A Prospective First-In-Human Study to Evaluate the Safety and Tolerability of QR-1123 in Subjects With Autosomal Dominant Retinitis Pigmentosa (adRP) Due to the P23H Mutation in the RHO Gene |
Year | 2019 |
Country | United States |
Company sponsor | ProQR Therapeutics |
Other ID(s) | PQ-1123-001 |
Vector information | |||
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Cohort 1 | |||||
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