Basic Information

Gene symbol AR Synonyms AIS, AR8, DHTR, HUMARA, HYSP1, KD, NR3C4, SBMA, SMAX1, TFM Type of gene protein-coding
Gene perturbation-related omics dataset PerturbAtlas | PertOrg
Description androgen receptor

GTO ID GTC1794
Trial ID NCT03300505
Disease Prostate Cancer
Altered gene AR
Therapeutic/Target gene Target gene
TherapyASO
Treatment AZD5312|ISIS 560131|ARRx
Co-treatment Enzalutamide
PhasePhase1
Recruitment statusTerminated
TitleARRO-CITO: (UMCC 2017.055) Phase Ib/II Single-Arm Multi-Center Study of IONIS-AR-2.5Rx, a Next Generation Androgen Receptor Antisense Oligonucleotide, in Combination With Enzalutamide in Metastatic Castration Resistant Prostate Cancer
Year2019
CountryUnited States
Company sponsorUniversity of Michigan Rogel Cancer Center
Other ID(s)UMCC 2017.055|HUM00130051
Vector information
VectorNo vector was used

Clinical Result

Cohort 1
Administration route intravenous injection|oral
Dosage ARRx, on Days 1, 4, 8, 11, 15 on cycle 1, then on days 1, 8, 15 in subsequent 21-day cycles|Enzalutamide, daily in 21 day cycles starting Day 1 of cycle 1
Pts 9
Age Adult, Older_Adult

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