Basic Information

Gene symbol FURIN Synonyms FUR, PACE, PCSK3, SPC1 Type of gene protein-coding
Gene perturbation-related omics dataset PerturbAtlas | PertOrg
Description furin, paired basic amino acid cleaving enzyme

Gene symbol TGFB1 Synonyms CED, DPD1, IBDIMDE, LAP, TGF-beta1, TGFB, TGFbeta Type of gene protein-coding
Gene perturbation-related omics dataset PerturbAtlas | PertOrg
Description transforming growth factor beta 1

Gene symbol TGFB2 Synonyms G-TSF, LDS4, TGF-beta2 Type of gene protein-coding
Description transforming growth factor beta 2

GTO ID GTC1341
Trial ID NCT01061840
Disease Ewing Sarcoma | Liver Cancer | Lung Non-Small Cell Carcinoma
Altered gene FURIN|TGFB1|TGFB2
Therapeutic/Target gene Target gene
TherapyshRNA
Treatment Vigil|FANG Vaccine
PhasePhase1
Recruitment statusCompleted
TitlePhase I Trial of Bi-shRNAfurin and GMCSF Augmented Autologous Tumor Cell Vaccine for Advanced Cancer
Year2009
CountryUnited States
Company sponsorGradalis, Inc.
Other ID(s)CL-PTL-101

Clinical Result

Cohort1: Vigil_dose level 2
Administration route intradermal injection
Dosage Vigil, 1E7 cells/injection
Age Child, Adult, Older_Adult
Cohort2: Vigil_dose level 3
Administration route intradermal injection
Dosage Vigil, 2.5E7 cells/injection
Age Child, Adult, Older_Adult
Cohort3: Vigil_dose level 1
Administration route intradermal injection
Dosage Vigil, 1E6 or 4E6 cells/injection
Age Child, Adult, Older_Adult

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