| Gene symbol | RPGR | Synonyms | COD1, CORDX1, CRD, PCDX, RP15, RP3, XLRP3, orf15 | Type of gene | protein-coding |
| Chromosome | X | Map location | Xp11.4 | dbXrefs | |
| Description | retinitis pigmentosa GTPase regulator | ||||
| GTO ID | GTC0659 |
| Trial ID | 2018-000425-31 |
| Disease | Retinitis Pigmentosa |
| Altered gene | RPGR |
| Therapeutic/Target gene | Therapeutic gene |
| Therapy | Gene transfer |
| Treatment | AAV2/5-hRKp.RPGR |
| Phase | Phase1|Phase2 |
| Recruitment status | Unknown |
| Title | Long term follow-up study of participants following an open label, multicentre, Phase I/II dose escalation trial of a recombinant adeno-associated virus vector (AAV2/5-hRKp.RPGR) for gene therapy of adults and children with X-linked Retinitis Pigmentosa owing to defects in Retinitis Pigmentosa GTPase Regulator (RPGR) |
| Year | 2018 |
| Country | United Kingdom |
| Company sponsor | MeiraGTx UK II Ltd |
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| Cohort 1 | |||||||
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